PERLARA
Perlara, PBC is the first Public Benefit Corporation accelerating precision drug discovery for 5,000+ rare genetic diseases. PLab uses a platform of CRISPR-engineered animal models (yeast, nematodes, fruit flies and zebrafish) in whole-organism phenotypic screens to generate disease-reversing orphan drug candidates much faster and cheaper than traditional in vitro and cell-based approaches. Their lead discovery programs are Niemann-Pick Type C, a lysosomal storage disorder first described nearly... a century ago, and NGLY1 Deficiency, a congenital disorder of glycosylation first diagnosed last year. Their initial pipeline includes, among others, additional lysosomal storage disorders, e.gs, Batten and Mucolipidosis IV, mitochondrial diseases, e.g., Leigh, and peroxisomal biogenesis disorders, e.g., Zellweger.
PERLARA
Industry:
Biotechnology Genetics Medical Pharmaceutical Therapeutics
Founded:
2014-02-01
Address:
San Francisco, California, United States
Country:
United States
Website Url:
http://www.perlara.com
Total Employee:
1+
Status:
Active
Contact:
+1 415 952 0559
Email Addresses:
[email protected]
Total Funding:
11.76 M USD
Technology used in webpage:
Viewport Meta IPhone / Mobile Compatible Apple Mobile Web Clips Icon Content Delivery Network Google Maps GStatic Google Static Content Sectigo SSL Sectigo Domain SSL Pound Sterling Wix
Current Advisors List
Current Employees Featured
Founder
Investors List
Homebrew
Homebrew investment in Series A - Perlara
Slow Ventures
Slow Ventures investment in Seed Round - Perlara
Y Combinator
Y Combinator investment in Seed Round - Perlara
Techammer
Techammer investment in Seed Round - Perlara
Travere Therapeutics
Travere Therapeutics investment in Seed Round - Perlara
Newest Events participated
Participated in Y Combinator Winter 2016 Demo Day
on 2016-03-22 as exhibitor
Official Site Inspections
http://www.perlara.com Semrush global rank: 2.31 M Semrush visits lastest month: 8.08 K
- Host name: unalocated.63.wixsite.com
- IP address: 185.230.63.171
- Location: Ashburn United States
- Latitude: 39.018
- Longitude: -77.539
- Metro Code: 511
- Timezone: America/New_York
- Postal: 20147
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